BOB体育

A Phase 2 Open-label Extension Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of AOC 1020 Administered Intravenously to Participants with Facioscapulohumeral Muscular Dystrophy (FSHD)

Investigator

Sub Subramony

Status

Accepting Candidates

Ages

16 Years - 70 Years

Sexes

All

The goal of this clinical trial is to test ATX-01 in participants with myotonic dystrophy type 1 (DM1). The main question it aims to answer is if ATX-01 is safe and well tolerated. The trial will compare the safety and tolerability of ATX-01 and a鈥�

Investigator

Sub Subramony

Status

Accepting Candidates

Ages

18 Years - 64 Years

Sexes

All

To evaluate the safety and tolerability, pharmacokinetics (PK), and pharmacodynamics (PD) of subcutaneous (SC) administration of CTI-1601 over 28 days in subjects with Friedreich's ataxia (FRDA).

Investigator

Sub Subramony

Status

Accepting Candidates

Ages

18 Years - N/A

Sexes

All